CD19 CAR-T Therapy for Lupus: Phase 1 Trial Results

by Archynetys Health Desk
  • Schett, G. et al. Advancements and challenges in CAR T cell therapy in autoimmune diseases. Nat. Rev. Rheumatol. 20531–544 (2024).

    PubMed

    Google Scholar

  • Müller, F. et al. CD19 CAR T-cell therapy in autoimmune disease—a case series with follow-up. N. Engl. J. Med. 390687–700 (2024).

    PubMed

    Google Scholar

  • Wang, W. et al. BCMA-CD19 compound CAR T cells for systemic lupus erythematosus: a phase 1 open-label clinical trial. Ann. Rheum. Dis. 831304–1314 (2024).

    CAS
    PubMed

    Google Scholar

  • Wang, X. et al. Allogeneic CD19-targeted CAR-T therapy in patients with severe myositis and systemic sclerosis. Cell 1874890–4904 (2024).

    CAS
    PubMed

    Google Scholar

  • Hoi, A., Igel, T., Mok, C. C. & Arnaud, L. Systemic lupus erythematosus. Lancet 4032326–2338 (2024).

    CAS
    PubMed

    Google Scholar

  • Liu, Y. et al. Chimeric STAR receptors using TCR machinery mediate robust responses against solid tumors. Sci. Transl. Med. 13eabb5191 (2021).

    CAS
    PubMed

    Google Scholar

  • Huang, D. et al. TCR-mimicking STAR conveys superior sensitivity over CAR in targeting tumors with low-density neoantigens. Cell Rep. 43114949 (2024).

    CAS
    PubMed

    Google Scholar

  • Wang, J. et al. A novel adoptive synthetic TCR and antigen receptor (STAR) T-cell therapy for B-cell acute lymphoblastic leukemia. Am. J. Hematol. 97992–1004 (2022).

    CAS
    PubMed

    Google Scholar

  • Aringer, M. et al. 2019 European League Against Rheumatism/American College of Rheumatology classification criteria for systemic lupus erythematosus. Ann. Rheum. Dis. 781151–1159 (2019).

    PubMed

    Google Scholar

  • Mikdashi, J. & Nived, O. Measuring disease activity in adults with systemic lupus erythematosus: the challenges of administrative burden and responsiveness to patient concerns in clinical research. Arthritis Res. Ther. 17183 (2015).

    PubMed
    PubMed Central

    Google Scholar

  • Petri, M. et al. Combined oral contraceptives in women with systemic lupus erythematosus. N. Engl. J. Med. 3532550–2558 (2005).

    CAS
    PubMed

    Google Scholar

  • Isenberg, D. A. et al. BILAG 2004. Development and initial validation of an updated version of the British Isles Lupus Assessment Group’s disease activity index for patients with systemic lupus erythematosus. Rheumatol. 44902–906 (2005).

    CAS

    Google Scholar

  • Furie, R. A. et al. Novel evidence-based systemic lupus erythematosus responder index. Arthritis Rheum. 611143–1151 (2009).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Jesus, D. et al. Systemic Lupus Erythematosus Disease Activity Score (SLE-DAS) enables accurate and user-friendly definitions of clinical remission and categories of disease activity. Ann. Rheum. Dis. 801568–1574 (2021).

    CAS
    PubMed

    Google Scholar

  • Gladman, D. D., Ibañez, D. & Urowitz, M. B. Systemic lupus erythematosus disease activity index 2000. J. Rheumatol. 29288–291 (2002).

    PubMed

    Google Scholar

  • Bajema, I. M. et al. Revision of the International Society of Nephrology/Renal Pathology Society classification for lupus nephritis: clarification of definitions, and modified National Institutes of Health activity and chronicity indices. Kidney Int. 93789–796 (2018).

    PubMed

    Google Scholar

  • Yee, C.-S. et al. Numerical scoring for the BILAG-2004 index. Rheumatol. 491665–1669 (2010).

    Google Scholar

  • Common Terminology Criteria for Adverse Events (CTCAE) v.5.0 (National Cancer Institute, 2017).

  • Lee, D. W. et al. ASTCT consensus grading for cytokine release syndrome and neurologic toxicity associated with immune effector cells. Biol. Blood Marrow Transplant. 25625–638 (2019).

    CAS
    PubMed

    Google Scholar

  • Harris, A. C. et al. International, multicenter standardization of acute graft-versus-host disease clinical data collection: a report from the Mount Sinai Acute GVHD International Consortium. Biol. Blood Marrow Transplant. 224–10 (2016).

    PubMed

    Google Scholar

  • Saad, A. et al. Hematopoietic cell transplantation, version 2.2020, NCCN Clinical Practice Guidelines in Oncology. J. Natl COMPR. Canc. Netw. 18599–634 (2020).

    CAS
    PubMed

    Google Scholar

  • Franklyn, K. et al. Definition and initial validation of a Lupus Low Disease Activity State (LLDAS). Ann. Rheum. Dis. 751615–1621 (2016).

    CAS
    PubMed

    Google Scholar

  • Bertsias, G. K. et al. Joint European League Against Rheumatism and European Renal Association-European Dialysis and Transplant Association (EULAR/ERA-EDTA) recommendations for the management of adult and paediatric lupus nephritis. Ann. Rheum. Dis. 711771–1782 (2012).

    CAS
    PubMed

    Google Scholar

  • Baker, K. F. et al. Single-cell insights into immune dysregulation in rheumatoid arthritis flare versus drug-free remission. Nat. Common. 151063 (2024).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Gong, T. & Zhou, R. ApoC3: an ‘alarmin’ triggering sterile inflammation. Nat. Immunol. 219–11 (2020).

    CAS
    PubMed

    Google Scholar

  • Huang, J.-Q. et al. SRPK1/AKT axis promotes oxaliplatin-induced anti-apoptosis via NF-κB activation in colon cancer. J. Transl. Med. 19280 (2021).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Zhang, J., Li, S., Liu, F. & Yang, K. Role of CD68 in tumor immunity and prognosis prediction in pan-cancer. Sci. Rep. 127844 (2022).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Cappell, K. M. & Kochenderfer, J. N. Long-term outcomes following CAR T cell therapy: what we know so far. Nat. Rev. Clin. Oncol. 20359–371 (2023).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Ghilardi, G. et al. T cell lymphoma and secondary primary malignancy risk after commercial CAR T cell therapy. Night. With. 30984–989 (2024).

    CAS
    PubMed

    Google Scholar

  • Qin, C. et al. Single-cell analysis of refractory anti-SRP necrotizing myopathy treated with anti-BCMA CAR-T cell therapy. Proc. Natl Acad. Sci. USA 121e2315990121 (2024).

    CAS
    PubMed Central

    Google Scholar

  • Qin, C. et al. Single-cell analysis of anti-BCMA CAR T cell therapy in patients with central nervous system autoimmunity. Sci. Immunol. 9eadj9730 (2024).

    CAS
    PubMed

    Google Scholar

  • Wu, C. et al. Single-cell transcriptomics reveal potent extrafollicular B cell response linked with granzyme K+ CD8 T cell activation in lupus kidney. Ann Rheum. Dis. 84451–466 (2025).

    Google Scholar

  • Moroni, G. et al. Lack of EULAR/ERA-EDTA response at 1 year predicts poor long-term renal outcome in patients with lupus nephritis. Ann. Rheum. Dis. 791077–1083 (2020).

    CAS
    PubMed

    Google Scholar

  • Anders, H.-J. et al. Lupus nephritis. Night. Rev. Haze. Primers 67 (2020).

    PubMed

    Google Scholar

  • Rovin, B. H. et al. KDIGO 2024 Clinical Practice Guideline for the management of lupus nephritis. Kidney Int. 105S1 -s69 (2024).

    Google Scholar

  • Fanouriakis, A. et al. EULAR recommendations for the management of systemic lupus erythematosus: 2023 update. Ann. Rheum. Dis. 8315–29 (2024).

    CAS
    PubMed

    Google Scholar

  • Li, H. & Durbin, R. Fast and accurate short read alignment with Burrows–Wheeler transform. Bioinformatics 251754–1760 (2009).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Wang, K., Li, M. & Hakonarson, H. ANNOVAR: functional annotation of genetic variants from high-throughput sequencing data. Nucleic Acids Res. 38e164 (2010).

    PubMed
    PubMed Central

    Google Scholar

  • Fan, H. C., Fu, G. K. & Fodor, S. P. Expression profiling. Combinatorial labeling of single cells for gene expression cytometry. Science 3471258367 (2015).

    PubMed

    Google Scholar

  • Wolf, F. A., Angerer, P. & Theis, F. J. SCANPY: large-scale single-cell gene expression data analysis. Genome Biol. 1915 (2018).

    PubMed
    PubMed Central

    Google Scholar

  • Wolock, S. L., Lopez, R. & Klein, A. M. Scrublet: computational identification of cell doublets in single-cell transcriptomic data. Cell Syst. 8281–291 (2019).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Korsunsky, I. et al. Fast, sensitive and accurate integration of single-cell data with Harmony. Nat. Methods 161289–1296 (2019).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Traag, V. A., Waltman, L. & van Eck, N. J. From Louvain to Leiden: guaranteeing well-connected communities. Sci. Rep. 95233 (2019).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Sturm, G. et al. Scirpy: a Scanpy extension for analyzing single-cell T-cell receptor-sequencing data. Bioinformatics 364817–4818 (2020).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Stewart, B. J. et al. Spatiotemporal immune zonation of the human kidney. Science 3651461–1466 (2019).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Kleshchevnikov, V. et al. Cell2location maps fine-grained cell types in spatial transcriptomics. Nat. Biotechnol. 40661–671 (2022).

    CAS
    PubMed

    Google Scholar

  • Zunder, E. R. et al. Palladium-based mass tag cell barcoding with a doublet-filtering scheme and single-cell deconvolution algorithm. Nat. Protoc. 10316–333 (2015).

    CAS
    PubMed
    PubMed Central

    Google Scholar

  • Finck, R. et al. Normalization of mass cytometry data with bead standards. Cytometry A 83483–494 (2013).

    PubMed
    PubMed Central

    Google Scholar

  • Fang, Z., Liu, X. & Peltz, G. GSEApy: a comprehensive package for performing gene set enrichment analysis in Python. Bioinformatics 39btac757 (2023).

    CAS
    PubMed

    Google Scholar

  • Related Posts

    Leave a Comment